Title	Authors	Journal/Conference	Year
Adeno-associated virus vector as a platform for gene therapy delivery	Wang D, Tai PWL, Gao G.	Nature Reviews Drug Discovery	2019
Gene Therapy Advances: A Meta-Analysis of AAV Usage in Clinical Settings	Au HKE, Isalan M, Mielcarek M	Frontiers in Medicine	2022
Current Clinical Applications of In Vivo Gene Therapy with AAVs	Mendell JR, Al-Zaidy SA, Rodino-Klapac LR, Goodspeed K, Gray SJ, Kay CN, Boye SL, Boye SE, George LA, Salabarria S, Corti M, Byrne BJ, Tremblay JP	Molecular Therapy	2021
Current progress and limitations of AAV mediated delivery of protein therapeutic genes and the importance of developing quantitative pharmacokinetic/pharmacodynamic (PK/PD) models	Chowdhury EA, Meno-Tetang G, Chang HY, Wu S, Huang HW, Jamier T, Chandran J, Shah DK	Advanced Drug Delivery Reviews	2021
Pharmaceutical Development of AAV-Based Gene Therapy Products for the Eye	Rodrigues GA, Shalaev E, Karami TK, Cunningham J, Slater NKH, Rivers HM	Pharmaceutical Research	2018
Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A	Ozelo MC, Mahlangu J, Pasi KJ, Giermasz A, Leavitt AD, Laffan M, Symington E, Quon DV, Wang JD, Peerlinck K, Pipe SW, Madan B, Key NS, Pierce GF, O'Mahony B, Kaczmarek R, Henshaw J, Lawal A, Jayaram K, Huang M, Yang X, Wong WY, Kim B	The New England Journal of Medicine	2022
Clinical Evidence Supporting Early Treatment Of Patients With Spinal Muscular Atrophy: Current Perspectives	Dangouloff T, Servais L	Therapeutics and Clinical Risk Management	2019